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Leber congenital amaurosis (LCA)

Showing 1 - 25 of 1,833

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To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

Not yet recruiting
  • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
  • (no location specified)
Aug 29, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong UniversitySch
Oct 12, 2023

Leber Congenital Amaurosis Trial in Shanghai (HG004)

Recruiting
  • Leber Congenital Amaurosis
  • HG004
  • Shanghai, Shanghai, China
    Xinhua Hospital affiliated with Shanghai Jiao Tong University Sc
Sep 26, 2023

Leber Congenital Amaurosis Trial (HG004)

Not yet recruiting
  • Leber Congenital Amaurosis
  • (no location specified)
Jun 13, 2023

Inherited Retinal Dystrophy Due to RPE65 Mutations, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia

Active, not recruiting
  • Inherited Retinal Dystrophy Due to RPE65 Mutations
  • Leber Congenital Amaurosis
  • AAV2-hRPE65v2,voretigene neparvovec-rzyl
  • Iowa City, Iowa
  • +1 more
Dec 9, 2021

Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)

Active, not recruiting
  • Leber Congenital Amaurosis 10
  • +9 more
  • Iowa City, Iowa
  • +2 more
Feb 8, 2022

Leber Congenital Amaurosis Trial in Ann Arbor, London (AAV RPE65)

Completed
  • Leber Congenital Amaurosis
  • AAV RPE65
  • Ann Arbor, Michigan
  • +1 more
Jun 17, 2021

Leber Congenital Amaurosis 10, Inherited Retinal Dystrophies, Eye Diseases, Hereditary Trial in United States (EDIT-101)

Active, not recruiting
  • Leber Congenital Amaurosis 10
  • +6 more
  • Miami, Florida
  • +4 more
Dec 2, 2022

Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen, Sham)

Active, not recruiting
  • Leber Congenital Amaurosis 10
  • +9 more
  • Iowa City, Iowa
  • +13 more
Mar 2, 2022

Leber Congenital Amaurosis Trial in Philadelphia (voretigene neparvovec-rzyl)

Completed
  • Leber Congenital Amaurosis
  • voretigene neparvovec-rzyl
  • Philadelphia, Pennsylvania
    The Children's Hospital of Philadelphia
Oct 30, 2020

Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis Trial in Worldwide (sepofarsen)

Recruiting
  • Leber Congenital Amaurosis 10
  • +10 more
  • Ghent, Belgium
  • +8 more
Mar 24, 2022

Leber's Congenital Amaurosis Trial in Iowa City, Philadelphia, Ghent (QR-110)

Completed
  • Leber's Congenital Amaurosis
  • Iowa City, Iowa
  • +2 more
Oct 13, 2020

Leber Congenital Amaurosis Associated With Mutations in RPE65

Recruiting
  • Leber Congenital Amaurosis
    • Ann Arbor, Michigan
    • +1 more
    Apr 7, 2022

    Natural History Study of CEP290-Related Retinal Degeneration

    Completed
    • Blindness
    • +7 more
      • Miami, Florida
      • +6 more
      May 18, 2022

      Amaurosis of Leber, Retinal Diseases Trial in Gainesville, Philadelphia (rAAV2-CBSB-hRPE65)

      Active, not recruiting
      • Amaurosis of Leber
      • Retinal Diseases
      • rAAV2-CBSB-hRPE65
      • Gainesville, Florida
      • +1 more
      Dec 13, 2021

      Cell Collection to Study Eye Diseases

      Recruiting
      • Retinal Disease
      • +3 more
        • Bethesda, Maryland
          National Institutes of Health Clinical Center
        Jan 23, 2023

        Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy Trial in United States (AAV2-hRPE65v2,voretigene

        Active, not recruiting
        • Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
        • AAV2-hRPE65v2,voretigene neparvovec-rzyl
        • Los Angeles, California
        • +9 more
        Oct 22, 2021

        Leber Congenital Amaurosis, Retinitis Pigmentosa Trial in Beijing (Human primary Retinal Pigment Epithelial (HuRPE) cells)

        Unknown status
        • Leber Congenital Amaurosis, Retinitis Pigmentosa
        • Human primary Retinal Pigment Epithelial (HuRPE) cells
        • Beijing, China
          Beijing Tongren Hospital
        Aug 7, 2018

        Rare Disorders, Undiagnosed Disorders, Disorders of Unknown Prevalence Trial in Sioux Falls, Sydney

        Recruiting
        • Rare Disorders
        • +309 more
          • Sioux Falls, South Dakota
          • +1 more
          Jun 20, 2022

          The Anatomical Localization of Inferior Mesenteric Artery in

          Recruiting
          • Rectal Cancer
          • measurement group
          • Xi'an, Shanxi, China
            General Surgery Gastriontestinal Department, Tang-Du of Fourth M
          Dec 13, 2022

          Blood Flow Path Reconstruction in Rectal Cancer

          Completed
          • Rectal Cancer
          • +2 more
          • no intervention
          • Jinan, Shandong, China
            Guoqin LIU
          Dec 21, 2022

          Clinical Presentation of Genetic Disorders in Patients Attending

          Not yet recruiting
          • Genetic Disease Clinical Presentation in Patients Attending Genetics Outpatient Clinic of Assiut University Children Hospital
            • (no location specified)
            Jun 2, 2023

            ACL, ACL Injury Trial in Bologna (Orthopure)

            Active, not recruiting
            • ACL
            • ACL Injury
            • Orthopure
            • Bologna, Italy
              IRCCS Istituto Ortopedico Rizzoli
            Oct 17, 2023

            Retinal Disorder Trial in New York (Placebos, ZA Low dose, ZA high dose)

            Suspended
            • Retinal Disorder
            • Placebos
            • +2 more
            • New York, New York
              NY NY
            Oct 7, 2020

            Choroideremia Trial in Edmonton (rAAV2.REP1 vector)

            Completed
            • Choroideremia
            • rAAV2.REP1 vector
            • Edmonton, Alberta, Canada
              University of Alberta
            May 16, 2022